Orphan Drugs & Rare Diseases

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We help you give new hope to those who are affected by rare diseases.
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Articles & Publications, Nazim Kanji, Huw Jones

Rare Diseases: Collaboration in Orphan, Rare and Pediatric Drug Development by Nazim Kanji and Huw Jones

By: Nazim Kanji Read More
What We Offer

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Drug Substance Synthesis & Manufacturing
Our drug substance capabilities including route scouting, PR&D, small-scale GMP manufacture, DOE/QbD, and 14C labeling.
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Translational Pharmaceutics®
Accelerates drug development by integrating real-time cGMP manufacturing and clinical activities.
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Clinical Pharmacology
Integrated first-in-human and clinical pharmacology programs that help you make critical decisions earlier.
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Drug Product Development & Manufacturing
Tailored drug product services from formulation development to clinical trial manufacturing and commercial production.
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Helping you bring new rare disease treatments to market, fast.

With integrated drug product development, clinical pharmacology, and drug product manufacturing services, we can help with the challenges associated with rare disease drug development.

Contact us today to learn how we can help your next drug program.

 

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